DelveInsight’s “Myotonic Dystrophy Market Insights, Epidemiology, and Market Forecast 2032” report delivers an in-depth understanding of the disease, historical and forecasted epidemiology, as well as the Myotonic Dystrophy market size, share, trends, and growth opportunities in the seven major markets (7MM) (i.e., the United States, EU4 (Germany, Spain, Italy, France), the United Kingdom and Japan).
The report covers emerging Myotonic Dystrophy drugs, current treatment practices, market share of individual therapies, and current & forecasted market size from 2019 to 2032. It also evaluates the current Myotonic Dystrophy treatment practice/algorithm, key drivers & barriers impacting the market growth, and unmet medical needs to curate the best of the opportunities and assess the underlying potential of the market.
Myotonic Dystrophy: An Overview
There are two main types of myotonic dystrophy (DM) — DM type 1 (DM1) and DM type 2 (DM2). DM1 is also known as Steinert disease, named after Dr. Steinert, who, along with colleagues, first described the classic form in the medical literature in 1909. DM2 is also known as Ricker syndrome proximal DM or PROMM. DM1 is further classified into congenital DM1, childhood DM1, adulthood DM1, and late-onset DM1.
DM1 and DM2 are caused by an expansion of DNA tandem repeats, resulting in an RNA gain of function mutation. DM1 is caused by the expansion of cytosine-thymine-guanine (CTG) repeat in the 3’-untranslated region of the DMPK gene on chromosome 19q13.3. DM2 results from the expansion of cytosine-cytosine-thymine-guanine (CCTG) tetranucleotide located in the intron of the CNB or ZNF9 gene on chromosome 3q21.3. DM1 is estimated to affect about 1 in 8,000–20,000 people in the general population. However, the prevalence of DM1 and DM2 varies greatly among different countries and ethnic groups.
Myotonic Dystrophy Market Key Facts
The total diagnosed prevalent patient population of Myotonic Dystrophy in the 7MM countries was close to 80,000 cases in 2021.
As per the estimates, the US had the highest patient population of Myotonic Dystrophy in 2021. Among the EU5 countries, Germany had the highest diagnosed patient population of Myotonic Dystrophy, with over 9,000 cases, followed by France in 2021.
On the other hand, Spain had the lowest diagnosed prevalent patient population of Myotonic Dystrophy, with approximately 6,000 cases in 2021.
Key players in the global Myotonic Dystrophy market include AMO Pharma Limited, Lupin Ltd., and Harmony Biosciences, LLC. The expected entry of promising agents, including tideglusib, DYNE-101, AOC 1001, pitolisant, and mexiletine, can transform the current standard of care and market of DM during the forecast period.
The market outlook section of the report helps to build a detailed comprehension of the historical, current, and forecasted market size by analyzing the impact of current and emerging Myotonic Dystrophy pipeline therapies. It also thoroughly assesses the Myotonic Dystrophy market drivers & barriers, unmet needs, and emerging technologies set to impact the market dynamics.
The report gives complete detail of the market trend for each marketed Myotonic Dystrophy drug and mid & late-stage pipeline therapies by evaluating their impact based on the annual cost of therapy, their Mechanism of Action (MOA), Route of Administration (ROA), molecule types, competition with other therapies, brand value, and their impact on the market.
Myotonic Dystrophy Epidemiology Assessment
The epidemiology section provides insights into the historical, current, and forecasted Myotonic Dystrophy epidemiology trends in the seven major countries (7MM) from 2019 to 2032. It helps to recognize the causes of current and forecasted Myotonic Dystrophy epidemiology trends by exploring numerous studies and research. The epidemiology section also provides a detailed analysis of diagnosed and prevalent patient pools, future trends, and views of key opinion leaders.
The Report Covers the Myotonic Dystrophy Epidemiology, Segmented as –
The diagnosed prevalent cases of Myotonic Dystrophy
Type-specific diagnosed cases of Myotonic Dystrophy
Type-specific diagnosed cases of DM1
Age-specific diagnosed cases of DM
Comorbidity associated with diagnosed cases of Myotonic Dystrophy
Myotonic Dystrophy Drugs Uptake and Pipeline Development Activities
The drug uptake section focuses on the uptake rate of potential drugs recently launched in the Myotonic Dystrophy market or expected to be launched during the study period. The analysis covers the Myotonic Dystrophy market uptake by drugs, patient uptake by therapies, and sales of each drug. Moreover, the therapeutics assessment section helps understand the market dynamics by drug sales, the most rapid drug uptake, and the reasons behind the maximal use of particular drugs. Additionally, it compares the Myotonic Dystrophy drugs based on their sale and market share.
The report also covers the Myotonic Dystrophy pipeline development activities. It provides valuable insights about different therapeutic candidates in various stages and the key Myotonic Dystrophy companies involved in developing targeted therapeutics. It also analyzes recent developments such as collaborations, acquisitions, mergers, licensing patent details, and other information for emerging therapies.
Learn How the Myotonic Dystrophy Market Will Evolve and Grow by 2032 @
Myotonic Dystrophy Therapeutics Analysis
Currently, no approved treatment offers a permanent cure for Myotonic Dystrophy, but researchers are studying ways to help people with these disorders. Present treatment is directed toward the specific symptoms that are apparent in each individual. Therapeutic options include Pharmacological management, rehabilitative therapy, medical devices, and surgical procedures, which can be varied based on the severity of symptoms.
Several major pharma and biotech companies developing therapies for Myotonic Dystrophy. Currently, AMO Pharma is leading the therapeutics market with its Myotonic Dystrophy drug candidates in the most advanced stage of clinical development.
Myotonic Dystrophy Companies Actively Working in the Therapeutics Market Include
And Many Others
Emerging and Marketed Myotonic Dystrophy Therapies Covered in the Report Include:
Tideglusib: AMO Pharma
Pitolisant: Harmony Biosciences
DYNE-101: Dyne Therapeutics
Mexiletine: Lupin Ltd.
And Many More
The Report Covers an In-depth Assessment of Emerging Drugs and key Companies. Download the Sample Report to Learn More @
Table of Content (TOC)
1. Key Insights
2. Executive Summary
3. Myotonic Dystrophy Competitive Intelligence Analysis
4. Myotonic Dystrophy Market Overview at a Glance
5. Myotonic Dystrophy Disease Background and Overview
6. Myotonic Dystrophy Patient Journey
7. Myotonic Dystrophy Patient Population and Epidemiology Trends (In the US, EU5, and Japan)
8. Myotonic Dystrophy Treatment Algorithm, Current Treatment, and Medical Practices
9. Myotonic Dystrophy Unmet Needs
10. Key Endpoints of Myotonic Dystrophy Treatment
11. Myotonic Dystrophy Marketed Therapies
12. Myotonic Dystrophy Emerging Drugs and Latest Therapeutic Advances
13. Myotonic Dystrophy Seven Major Market Analysis
14. Attribute Analysis
15. Myotonic Dystrophy Market Outlook (In US, EU5, and Japan)
16. Myotonic Dystrophy Companies Active in the Market
17. Myotonic Dystrophy Access and Reimbursement Overview
18. KOL Views on the Myotonic Dystrophy Market
19. Myotonic Dystrophy Market Drivers
20. Myotonic Dystrophy Market Barriers
22. DelveInsight Capabilities
*The Table of Contents (TOC) is not exhaustive; the final content may vary. Refer to the sample report for the complete table of contents.
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